MPS VI临床试验

粘多糖病(MPS VI), 也被称为马罗托-拉米综合征, 遗传性溶酶体贮积症是由于缺乏分解某些复杂碳水化合物所需的酶引起的吗.

了解澳门正规博彩十大排行平台的MPS VI临床试验如下.

Galsulfase

学习MPSVI CSP 完整的

粘多糖病(MPS) VI临床监测项目(CSP)

观点研究

指示

粘多糖病VI (MPS VI, Maroteaux-Lamy综合征)

目标

The objectives of this program are: to further characterize the natural progression of MPS VI disease; to generate and disseminate information on the care and management of MPS VI patients to clinical and medical professionals; to provide a resource to physicians and patients by providing information for optimizing patient care based on aggregate data; to characterize the clinical response to long-term galsulfase treatment; to further characterize the long-term safety of galsulfase treatment.

临床实验的治疗

Galsulfase

状态

本研究已经完成

研究类型

第四阶段